Recent News and Updates
They Said “Yes” to Gene Therapy
By Rhonda Rowland We continue the story of two trailblazers who are among the first Wilson disease (WD) patients to volunteer for one of the two gene therapy clinical trials now underway for our [...]
Ultragenyx Wilson Disease Update August 2023
On behalf of the Ultragenyx Wilson disease study team, we would like to share an update on our CYPRUS2+ study. […]
How Mark Cuban helped a Cherry Hill business exec cut prices for the drug that keeps him alive
For decades, the drug that keeps Drew Katz alive sold for less than $1 a pill. […]
WD Low Cost Drugs
Read the press release.
Request for Volunteers
Vivet Therapeutics, a biotechnology company researching a potential treatment for Wilson disease, is looking to speak with patients and caregivers in the Wilson disease community. Read More
Alexion’s Wilson Disease Drug Program Terminated
April 28, 2023 The Wilson Disease Association (WDA) is disappointed to share that Alexion, AstraZeneca Rare Disease decided to terminate its ALXN1840 program. Alexion pursued rigorous scientific research in its effort to bring forward a [...]
