Recent News and Updates
How Mark Cuban helped a Cherry Hill business exec cut prices for the drug that keeps him alive
For decades, the drug that keeps Drew Katz alive sold for less than $1 a pill. […]
WD Low Cost Drugs
Read the press release.
Alexion’s Wilson Disease Drug Program Terminated
April 28, 2023 The Wilson Disease Association (WDA) is disappointed to share that Alexion, AstraZeneca Rare Disease decided to terminate its ALXN1840 program. Alexion pursued rigorous scientific research in its effort to bring forward a [...]
New Drug Launched
Orphalan announces US commercial launch of Cuvrior™ for the treatment of Wilson disease. Read the press release.
A New Guidance on Wilson Disease
Diagnosis|Treatment|Monitoring By Rhonda Rowland This is a first for Wilson disease (WD). The new Practice Guidance on WD is a careful balance of combining limited scientific evidence with expert experience to create a tool for [...]
Ultragenyx’s Wilson Disease Gene Therapy Program Update
On behalf of the Ultragenyx Wilson disease study team, we would like to share a recent update on our CYPRUS2+ study. Ultragenyx has changed Stage 1 of our CYPRUS2+ study to an open-label, single [...]
