Recent News and Updates
WDA designates newest Wilson Disease Center of Excellence at University of California, Davis
Read more: https://health.ucdavis.edu/news/headlines/uc-davis-health-designated-wilson-disease-center-of-excellence/2024/09
Ultragenyx Wilson Disease Update April 2024
As Ultragenyx continues to advance its research for Wilson disease, please find a status update on the CYPRUS2+ study. The CYPRUS2+ study is designed with three stages. We are currently in Stage 1 where [...]
One Step Closer to a Newborn Screening Test for Wilson Disease
Key Proteo Submits De Novo Application to FDA for its First Newborn Screening Kit Potential to be the first IVD for the screening of Wilson Disease, Wiskott-Aldrich Syndrome, X-linked Agammaglobulinemia and Adenosine Deaminase Deficiency [...]
Ultragenyx Wilson Disease Gene Therapy Trial Update for WDA
As requested, we are providing an update on Stage 1 of our Cyprus2+ study, assessing safety and efficacy of UX701, an investigational gene therapy for the treatment of Wilson disease. The status update below [...]
Wilson Disease Reviewed in Top Medical Journal
The Wilson Disease Association (WDA) is excited to share that the review article, “Current and Emerging Issues in Wilson’s Disease,” by Dr. Eve Roberts and Dr. Michael Schilsky is published in this week’s New [...]
Ultragenyx Wilson Disease Update August 2023
On behalf of the Ultragenyx Wilson disease study team, we would like to share an update on our CYPRUS2+ study. […]
