Genetic Therapies

Genetic therapies for Wilson Disease have been planned for several years. There are several companies working on variations of genetic therapies. Vivet started recruiting for clinical trials in spring of 2021. For more information on clinical trials go to

Brochures provided by companies working on genetic therapies are below for you to view or download.

The following companies presented at the Wilson Disease Association virtual conference in 2020. 
They are taking different approaches to genetic therapies.
Ultragenyx: Watch on Youtube
Deep Genomics: Watch on Youtube


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